Epidiolex reduced key seizures by 17-23% more than placebo in children with severe epilepsy

A clinical pharmacology review of Epidiolex (pure plant-derived CBD) found it reduced convulsive seizures in Dravet and drop seizures in Lennox-Gastaut by 17-23% over placebo, with important drug interactions with clobazam and valproate.

Chen, Jeffrey W et al.·The Annals of pharmacotherapy·2019·Strong EvidenceReview
RTHC-01980ReviewStrong Evidence2019RETHINKTHC RESEARCH DATABASErethinkthc.com/research

Quick Facts

Study Type
Review
Evidence
Strong Evidence
Sample
Not reported

What This Study Found

In the GWPCARE trial series, CBD reduced key seizure frequencies by 17-23% compared to placebo as adjunctive therapy in patients 2+ years old. Common adverse effects: somnolence, diarrhea, elevated liver enzymes. Important drug interactions with clobazam, valproates, and CYP2C19/3A4 inhibitors/inducers. This is the first cannabis-derived FDA-approved medication.

Key Numbers

Seizure reduction: 17-23% over placebo. Approved for patients 2+ years old. Key interactions: clobazam, valproates, CYP2C19 and CYP3A4 modulators. Adverse effects: somnolence, diarrhea, hepatic transaminase elevations.

How They Did This

Review of EMBASE and MEDLINE (1946-October 2018) plus product labeling and ClinicalTrials.gov for efficacy, safety, pharmacology, and pharmacokinetics of Epidiolex in Dravet and Lennox-Gastaut syndromes.

Why This Research Matters

This clinical pharmacy-focused review provides the practical dosing, monitoring, and interaction information clinicians need to safely prescribe CBD for epilepsy, going beyond efficacy to address real-world implementation.

The Bigger Picture

Epidiolex approval created a new category of prescription drug that requires clinicians to understand cannabinoid pharmacology. This review bridges the gap between the clinical trial data and day-to-day prescribing decisions.

What This Study Doesn't Tell Us

Approved for only two epilepsy syndromes. Long-term safety data still accumulating. Drug interactions complicate use in patients on multiple anti-epileptic drugs. Mechanism of action remains hypothesized, not confirmed.

Questions This Raises

  • ?Will CBD gain approval for additional epilepsy syndromes?
  • ?How should hepatic monitoring be optimized?
  • ?Can drug interaction management be standardized?

Trust & Context

Key Stat:
17-23% over placebo
Evidence Grade:
Rated strong because the review is based on Phase III GWPCARE RCTs that led to FDA approval.
Study Age:
Published in 2019, shortly after FDA approval of Epidiolex.
Original Title:
Cannabidiol: A New Hope for Patients With Dravet or Lennox-Gastaut Syndromes.
Published In:
The Annals of pharmacotherapy, 53(6), 603-611 (2019)
Database ID:
RTHC-01980

Evidence Hierarchy

Meta-Analysis / Systematic Review
Randomized Controlled Trial
Cohort / Case-Control
Cross-Sectional / ObservationalSnapshot without intervening
This study
Case Report / Animal Study

Summarizes existing research on a topic.

What do these levels mean? →

Frequently Asked Questions

How effective is Epidiolex?

It reduced convulsive seizures (Dravet) and drop seizures (Lennox-Gastaut) by 17-23% more than placebo, on top of standard anti-epileptic drugs.

What drug interactions should be watched?

Clobazam, valproates, and drugs that affect CYP2C19 and CYP3A4 enzymes. Liver function monitoring is important, especially with concurrent valproate use.

Read More on RethinkTHC

Cite This Study

RTHC-01980·https://rethinkthc.com/research/RTHC-01980

APA

Chen, Jeffrey W; Borgelt, Laura M; Blackmer, Allison B. (2019). Cannabidiol: A New Hope for Patients With Dravet or Lennox-Gastaut Syndromes.. The Annals of pharmacotherapy, 53(6), 603-611. https://doi.org/10.1177/1060028018822124

MLA

Chen, Jeffrey W, et al. "Cannabidiol: A New Hope for Patients With Dravet or Lennox-Gastaut Syndromes.." The Annals of pharmacotherapy, 2019. https://doi.org/10.1177/1060028018822124

RethinkTHC

RethinkTHC Research Database. "Cannabidiol: A New Hope for Patients With Dravet or Lennox-G..." RTHC-01980. Retrieved from https://rethinkthc.com/research/chen-2019-cannabidiol-a-new-hope

Access the Original Study

Study data sourced from PubMed, a service of the U.S. National Library of Medicine, National Institutes of Health.

This study breakdown was produced by the RethinkTHC research team. We analyze and report published research findings without making health recommendations. All interpretations are based solely on the published abstract and study data.