Purified CBD reduced seizures in 38% of children with severe epilepsy

In 29 pediatric patients with severe developmental and epileptic encephalopathy, artisanal CBD oil reduced seizure frequency by 50% or more in 38% of patients, with one becoming seizure-free.

Pietrafusa, Nicola et al.·Paediatric drugs·2019·Preliminary EvidencePilot Study
RTHC-02231Pilot StudyPreliminary Evidence2019RETHINKTHC RESEARCH DATABASErethinkthc.com/research

Quick Facts

Study Type
Pilot Study
Evidence
Preliminary Evidence
Sample
N=29

What This Study Found

Eleven of 29 patients (37.9%) achieved 50% or greater seizure reduction. One patient became seizure-free. No patients experienced worsening seizure frequency. Adverse effects were reported in 7 patients (24%), mostly somnolence, decreased appetite, and diarrhea, all mild and transient.

Key Numbers

29 patients enrolled. 41.4% male. Mean age: 9.3 years (range 1.9-16.3). Mean CBD exposure: 11.2 months. 37.9% had 50%+ seizure reduction. 1 patient seizure-free. 62.1% had no benefit. 24.1% had mild adverse effects.

How They Did This

Single-center, prospective, open-label study at Bambino Gesu Children's Hospital in Rome. Patients aged 1-18 with treatment-refractory developmental and epileptic encephalopathy received purified CBD oil (98-99% pure) at 2-25 mg/kg/day added to existing antiepileptic drugs for at least 6 months.

Why This Research Matters

Pharmaceutical-grade CBD (Epidiolex) was approved in the US for Dravet and Lennox-Gastaut syndromes but was not available internationally. This study tested artisanal purified CBD in a broader range of severe epilepsies, showing potential benefit beyond the approved indications.

The Bigger Picture

This adds to the growing evidence that CBD has anti-seizure properties across multiple epilepsy types, not just the two FDA-approved indications. The high rate of non-responders (62%) also underscores that CBD is not a universal epilepsy treatment.

What This Study Doesn't Tell Us

Open-label study with no placebo group or blinding. Small sample size. Artisanal formulation, not pharmaceutical-grade. All patients were on concurrent antiepileptic drugs.

Questions This Raises

  • ?Which epilepsy subtypes respond best to CBD?
  • ?Could higher doses or different formulations improve the response rate?
  • ?Are the non-responders fundamentally different from responders?

Trust & Context

Key Stat:
38% of patients achieved 50%+ seizure reduction
Evidence Grade:
Preliminary: open-label pilot study with no control group, though the 6-month duration adds value.
Study Age:
Published in 2019.
Original Title:
Purified Cannabidiol for Treatment of Refractory Epilepsies in Pediatric Patients with Developmental and Epileptic Encephalopathy.
Published In:
Paediatric drugs, 21(4), 283-290 (2019)
Database ID:
RTHC-02231

Evidence Hierarchy

Meta-Analysis / Systematic Review
Randomized Controlled Trial
Cohort / Case-Control
Cross-Sectional / ObservationalSnapshot without intervening
This study
Case Report / Animal Study

A small preliminary study to test whether a larger study is feasible.

What do these levels mean? →

Frequently Asked Questions

Is this the same as Epidiolex?

No. Epidiolex is a pharmaceutical-grade CBD product approved by the FDA. This study used an artisanal 98-99% pure CBD oil formulation available in Italy.

Why didn't CBD help all the children?

Epilepsy is highly heterogeneous, and different seizure types respond to different treatments. The 62% non-response rate is consistent with other epilepsy treatments and highlights the need to identify which patients are most likely to benefit.

Read More on RethinkTHC

Cite This Study

RTHC-02231·https://rethinkthc.com/research/RTHC-02231

APA

Pietrafusa, Nicola; Ferretti, Alessandro; Trivisano, Marina; de Palma, Luca; Calabrese, Costanza; Carfì Pavia, Giusy; Tondo, Ilaria; Cappelletti, Simona; Vigevano, Federico; Specchio, Nicola. (2019). Purified Cannabidiol for Treatment of Refractory Epilepsies in Pediatric Patients with Developmental and Epileptic Encephalopathy.. Paediatric drugs, 21(4), 283-290. https://doi.org/10.1007/s40272-019-00341-x

MLA

Pietrafusa, Nicola, et al. "Purified Cannabidiol for Treatment of Refractory Epilepsies in Pediatric Patients with Developmental and Epileptic Encephalopathy.." Paediatric drugs, 2019. https://doi.org/10.1007/s40272-019-00341-x

RethinkTHC

RethinkTHC Research Database. "Purified Cannabidiol for Treatment of Refractory Epilepsies ..." RTHC-02231. Retrieved from https://rethinkthc.com/research/pietrafusa-2019-purified-cannabidiol-for-treatment

Access the Original Study

Study data sourced from PubMed, a service of the U.S. National Library of Medicine, National Institutes of Health.

This study breakdown was produced by the RethinkTHC research team. We analyze and report published research findings without making health recommendations. All interpretations are based solely on the published abstract and study data.