CBD Reduced Seizures in 5 of 6 Patients With a Rare Genetic Epilepsy

Five of six patients with drug-resistant epilepsy caused by rare GPI-anchored protein deficiencies responded to purified CBD, with an 83% responder rate sustained over a median of 27 months.

Riva, Antonella et al.·Cannabis and cannabinoid research·2024·PreliminaryCase Report
RTHC-05655Case ReportPreliminary2024RETHINKTHC RESEARCH DATABASErethinkthc.com/research

Quick Facts

Study Type
Case Report
Evidence
Preliminary
Sample
Not reported

What This Study Found

Six patients with genetically confirmed GPI-anchored protein deficiency and drug-resistant epilepsy received add-on CBD (Epidyolex). At 12 months, 5 of 6 (83%) were responders. No severe adverse events. Mean CBD dose was 17.85 mg/kg/day.

Key Numbers

6 patients; 83% responders at 12 months; mean dose 17.85 mg/kg/day; median treatment duration 27 months; no severe adverse events.

How They Did This

Case series of 6 patients with genetically proven GPI-anchored protein deficiency epilepsy treated with pharmaceutical-grade CBD as add-on therapy.

Why This Research Matters

GPI-anchored protein deficiencies cause severe, drug-resistant epilepsy with few treatment options. An 83% response rate suggests a potential targeted therapy.

The Bigger Picture

CBD is approved for specific epilepsy syndromes, but many rare genetic epilepsies remain without evidence-based treatments. This small series suggests GPI-related epilepsy may be another responsive condition.

What This Study Doesn't Tell Us

Only 6 patients. No placebo control. Ultra-rare condition limits replication possibilities.

Questions This Raises

  • ?Is there a mechanistic explanation for why GPI-deficiency epilepsy responds to CBD?
  • ?Would larger registries confirm these response rates?

Trust & Context

Key Stat:
83% responder rate at 12 months
Evidence Grade:
Very small case series in an ultra-rare condition. Encouraging but cannot establish efficacy.
Study Age:
2024 publication
Original Title:
Cannabidiol Add-On in Glycosylphosphatidylinositol-Related Drug-Resistant Epilepsy.
Published In:
Cannabis and cannabinoid research, 9(4), 990-995 (2024)
Database ID:
RTHC-05655

Evidence Hierarchy

Meta-Analysis / Systematic Review
Randomized Controlled Trial
Cohort / Case-Control
Cross-Sectional / ObservationalSnapshot without intervening
This study
Case Report / Animal Study
What do these levels mean? →

Frequently Asked Questions

Can CBD help with rare genetic epilepsy?

In this small study, 5 of 6 patients with epilepsy caused by GPI-anchored protein deficiency responded to purified CBD, with sustained seizure reduction over a median of 27 months.

How long does CBD take to work for epilepsy?

Response was assessed at 12 months, with all 5 responders maintaining benefit through the median 27-month follow-up. CBD was titrated from 2 mg/kg/day up to a median of 25 mg/kg/day.

Read More on RethinkTHC

Cite This Study

RTHC-05655·https://rethinkthc.com/research/RTHC-05655

APA

Riva, Antonella; D'Onofrio, Gianluca; Pisati, Angelica; Roberti, Roberta; Amadori, Elisabetta; Bosch, Friedrich; de Souza, Carolina Fischinger Moura; Thomas, Ashley; Russo, Emilio; Striano, Pasquale; Bayat, Allan. (2024). Cannabidiol Add-On in Glycosylphosphatidylinositol-Related Drug-Resistant Epilepsy.. Cannabis and cannabinoid research, 9(4), 990-995. https://doi.org/10.1089/can.2022.0255

MLA

Riva, Antonella, et al. "Cannabidiol Add-On in Glycosylphosphatidylinositol-Related Drug-Resistant Epilepsy.." Cannabis and cannabinoid research, 2024. https://doi.org/10.1089/can.2022.0255

RethinkTHC

RethinkTHC Research Database. "Cannabidiol Add-On in Glycosylphosphatidylinositol-Related D..." RTHC-05655. Retrieved from https://rethinkthc.com/research/riva-2024-cannabidiol-addon-in-glycosylphosphatidylinositolrelated

Access the Original Study

Study data sourced from PubMed, a service of the U.S. National Library of Medicine, National Institutes of Health.

This study breakdown was produced by the RethinkTHC research team. We analyze and report published research findings without making health recommendations. All interpretations are based solely on the published abstract and study data.